Meet Our Faculty
| Core Faculty | ||
| Gene Therapy Interest | ||
| Allison Bradbury, PhD | CNS | Laboratory |
| Anne Connolly, MD | Neuromuscular | Clinical |
| Kevin Flanigan, MD | CNS; Neuromuscular | Clinical, Laboratory |
| Scott Harper, PhD | Neuromuscular | Laboratory |
| Stephen Kaler, MD | Genetics, Copper Metabolism | Clinical, Laboratory |
| Paul Martin, PhD | Neuromuscular | Laboratory |
| Jerry R. Mendell, MD | Neuromuscular | Clinical, Laboratory |
| Kathrin Meyer, PhD | CNS; Neuromuscular | Laboratory |
| Afrooz Rashnonejad, PhD | Neuromuscular | Laboratory |
| Zarife Sahenk, MD, PhD | Neuromuscular | Clinical, Laboratory |
| Sriram Vaidyanathan, PhD | Genome Editing, Cystic Fibrosis | Laboratory |
| Megan Waldrop, MD | Neuromuscular | Clinical |
| Nicolas Wein, PhD | CNS; Neuromuscular | Laboratory |