Center for Gene Therapy
The mission of the Center for Gene Therapy is to investigate and employ the use of gene and cell based therapeutics for prevention and treatment of human diseases including: neuromuscular and neurodegenerative diseases, lysosomal storage disorders, ischemia and re-perfusion injury, neonatal hypertension, cancer and infectious diseases.
Meet Our Team
Learn more about director Kevin Flanigan, MD, and his team of principal investigators at the Center for Gene Therapy.
Gene Therapy Research and Projects
Learn more about the areas of focus at the Center for Gene Therapy and see the latest featured research and projects to come out of our center.
NIH/NIAMS Center of Research Translation in Muscular Dystrophy
The Center for Gene Therapy has a dedicated translational program that targets muscular dystrophies, with a particular longstanding interest in developing meaningful therapies for the most common forms.
Muscular Dystrophy Research
Dr. Jerry Mendell and his team have discovered that gene therapy can treat the underlying cause of muscular dystrophy - something that other drugs and medications can't currently do.
Nationwide Children’s Hospital is not only home to world-class neuromuscular research and clinical services, it’s also the hub of an extraordinary collaborative environment.
Annual Myology Training Course
The Myology Course at Nationwide Children's is the only U.S. workshop of its kind, featuring a mix of basic and clinical science lectures followed by specific training in either clinical treatment protocols or basic science laboratory techniques.
OSU and Nationwide Children's Muscle Group
The OSU and Nationwide Children's Muscle Group brings together investigators with diverse research interests in skeletal muscle, cardiac muscle, and neuromuscular biology.
The Research Institute at Nationwide Children’s Hospital is the home to a current Good Manufacturing Practices (cGMP) Clinical Manufacturing Faculty that operates according to FDA cGMP Guidelines to ensure the safety of manufactured biologic products.