Center for Gene Therapy
The mission of the Center for Gene Therapy is to investigate and employ the use of gene and cell based therapeutics for prevention and treatment of human diseases including: neuromuscular and neurodegenerative diseases, lysosomal storage disorders, ischemia and re-perfusion injury, neonatal hypertension, cancer and infectious diseases.
Meet Our Team
Learn more about director Kevin Flanigan, MD, and his team of principal investigators at the Center for Gene Therapy.
Under the direction of Kevin Flanigan, MD, the Flanigan Lab focuses on the genetic and molecular characterization of inherited neuromuscular diseases, and toward the development of therapies directed toward these diseases.
The Myology Course at Nationwide Children's is the only U.S. workshop of its kind, featuring a mix of basic and clinical science lectures followed by specific training in either clinical treatment protocols or basic science laboratory techniques.
"This Month in Muscular Dystrophy"
Hosted by Kevin Flanigan, MD, "This Month in Muscular Dystrophy" podcasts highlight the latest in muscular dystrophy and other inherited neuromuscular disease research.
Muscular Dystrophy Research
Dr. Jerry Mendell and his team have discovered that gene therapy can treat the underlying cause of muscular dystrophy - something that other drugs and medications can't currently do.
Muscular Dystrophy Center
The Center of Research Translation (CORT) in Muscular Dystrophy Therapeutic Development makes use of the experience of institutional investigators in bringing AAV-based and other genetic therapies through preclinical development to investigator-sponsored and industry-partnered clinical trials.
Nationwide Children’s Hospital is not only home to world-class neuromuscular research and clinical services, it’s also the hub of an extraordinary collaborative environment.
OSU and Nationwide Children's Muscle Group
The OSU and Nationwide Children's Muscle Group brings together investigators with diverse research interests in skeletal muscle, cardiac muscle, and neuromuscular biology.