Providing Better Health Care for All Children
Our research translates to real-world solutions that benefit children everywhere.
Learn how our research – and the funding that supports it – improves the lives of children facing life-threatening health conditions.
Thanks to decades of research funded by the NIH, two of the first eight gene therapies ever approved by the FDA were developed here for Duchenne muscular dystrophy and spinal muscular atrophy.
Therapies for Rare Devastating Diseases
New Approaches for Advanced Cancer Care

An Important Collaboration Provides Cancer Patients With the Best Treatment Options
A collaborative vision for to offer patients precision cancer diagnoses and treatments between the Children’s Oncology Group, the National Cancer Institute and Nationwide Children’s Hospital is a reality.

Breaking New Ground in Cancer Care
Remarkable research supported by the NIH is merging immunology and gene therapy in a way that has not been done before to deliver safer, more efficient and patient-friendly cancer care.

Using the Body’s Immune System to Treat Cancer
Recent advances producing natural killer cells offers pediatric patients new hope for remission after high-risk cancer diagnoses, thanks to federally funded research.
Thanks to funding from the National Institute for Mental Health, behavioral health researchers are accelerating ways to prevent child and adolescent suicide.
Understanding What Works to Prevent Youth Suicide
Preventing and Treating Serious Childhood Illness

Groundbreaking Research to Treat the Worst Infections
NIH-funded research into the structure and function of bacterial biofilms have begun to pay off in the form of imminent clinical applications.

Probiotics: Preventing a Deadly Condition in Preterm Infants
Funding from the National Institute of General Medical Sciences at the NIH has supported this newborn research to prevent NEC, a deadly condition in preterm infants.

Replacement Blood Vessels That Grow With Children
For children with heart disease, this NIH-funded research improves their lives with engineered blood vessels.