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Kevin M Flanigan
Kevin M. Flanigan, MD, is an attending neurologist at Nationwide Children's and director of the Jerry R. Mendell Center for Gene Therapy in the Abigail Wexner Research Institute at Nationwide Children's Hospital.
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March 2013
Dr. Louise Rodino-Klapac discusses alpha 7 integrin as A therapeutic approach to muscular dystrophy.
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January 2015
Dr. Louise Rodino-Klapac discusses dysferlin overlap vectors to restore function in dysferlinopathies.
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Myology Course Archive
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Flanigan Lab
Under the direction of Kevin Flanigan, MD, the Flanigan Lab focuses on the genetic and molecular characterization of inherited neuromuscular diseases, and toward the development of therapies directed toward these diseases.
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February 2015
Dr. Kevin Flanigan discusses IRES-Induced Dystrophin as a potential therapy for DMD.
Project 2
Led by Kevin Flanigan, MD, Research Project 2 of our MDSRC Program has a long-term goal to develop vectors that maximize RNA splice alteration efficiency to provide the best potential outcome for individual patients.
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Gene Therapy Fellowship Application and Selection
Interested in applying for our Neuromuscular Genetic Therapeutics Fellowship? Learn more about our Neuromuscular Genetic Therapeutics Fellowship application and selection.
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Flanigan Named to Neuromuscular, Gene Therapy Leadership Roles
Beginning January 1, 2017, Kevin Flanigan, MD, will become the director of the Center for Gene Therapy and the Neuromuscular Disorders program at Nationwide Children’s Hospital. Dr.
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Cure Duchenne to Host a Webinar on Duplication Research for Duchenne Muscular Dystrophy with Dr. Kevin Flanigan from Nationwide Childrens Hospital on April 6
NEWPORT BEACH, Calif. -- CureDuchenne, a nonprofit that raises awareness and funds research to find a cure for Duchenne muscular dystrophy, will host an “Update on Duplication Mutation Research for Duchenne Muscular Dystrophy” webinar with Dr.
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July 2013
Dr. Jeff Chamberlain discusses gene and cell mediated therapies for muscular dystrophy.
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Resources
Check out our Neuromuscular Disorders Clinic resources including clinical trials, family services, organizations and podcasts.
About the MDSRC
Researchers in the Jerry R. Mendell, MD Center for Gene Therapy at Nationwide Children's Hospital have received a coveted P50 grant from the National Institutes of Health to establish a Wellstone Muscular Dystrophy Specialized Research Center (MDSRC). Named in honor of the late Senator Paul D.
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Nationwide Childrens CEO to Co-Chair Parent Project Muscular Dystrophy Event
Nationwide Children’s Hospital CEO Steve Allen, MD, will serve as co-chair of the first Transforming Duchenne Care workshop to be held June 27 and 28, 2012, in Ft. Lauderdale, FL.
Cores
The Nationwide Children's Hospital Wellstone Muscular Dystrophy Specialized Research Center contains the Cores that support its mission. The Administrative Core (Dr. Kevin Flanigan, director; Dr. Paul Martin, co-director; Ms.
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FDA Approves First Gene Therapy Treatment for SMA Developed at the Abigail Wexner Research Institute at Nationwide Children’s Hospital
Today, the Abigail Wexner Research Institute at Nationwide Children’s Hospital praised the Food and Drug Administration (FDA) for its approval of Zolgensma® for spinal muscular atrophy (SMA) following decades of research in its Center for Gene Therapy to help patients with neuromuscular diseases.
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Nationwide Childrens Hospital Neuromuscular Disorder Podcasts Now Available on iTunes
In 2010, the Center for Gene Therapy at Nationwide Children’s Hospital launched a monthly podcast entitled, “This Month in Muscular Dystrophy,” featuring internationally known scientists discussing the latest research in muscular dystrophy and other neuromuscular disorders.
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Nationwide Children’s Hospital Receives a Wellstone Muscular Dystrophy Specialized Research Center Award from the NIH
Researchers in the Jerry R. Mendell, MD Center for Gene Therapy at Nationwide Children's Hospital have received a coveted P50 grant from the National Institutes of Health to establish a Wellstone Muscular Dystrophy Specialized Research Center (MDSRC).
"This Month in Muscular Dystrophy"
Hosted by Kevin Flanigan, MD, "This Month in Muscular Dystrophy" podcasts highlight the latest in muscular dystrophy and other inherited neuromuscular disease research.
Meet Our Team
Learn more about director Kevin Flanigan, MD, and the team of principal investigators at the Jerry R. Mendell Center for Gene Therapy.
Meet Our Faculty
Core Faculty Gene Therapy Interest Allison Bradbury, PhD CNS Laboratory Anne Connolly, MD Neuromuscular Clinical Kevin Flanigan, MD CNS; Neuromuscular Clinical, Laboratory Scott Harper, PhD Neuromuscular Laboratory Stephen Kaler, MD Genetics, Copper Metabolism Clinical, Laboratory Paul Martin, PhD
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Fetal Research Affinity Group Members
The Fetal Research Affinity Group is made up of experts in fetal therapy, neonatology, genetics, molecular biology and others perinatal fields. Learn more about its members.
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Nationwide Childrens Hospital Neuromuscular Disease Researchers Receive $7.5 Million NIH Grant
The National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) of the National Institutes of Health announced four new Centers of Research Translation awards today.
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Gene Therapy and Neuromuscular Training
Nationwide Children’s Hospital is not only home to world-class neuromuscular research and clinical services, it’s also the hub of an extraordinary and collaborative training environment.
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FDA Approves First Gene Therapy Treatment for Duchenne Muscular Dystrophy Developed at the Abigail Wexner Research Institute at Nationwide Children’s Hospital
Today, the Abigail Wexner Research Institute at Nationwide Children’s Hospital praised the Food and Drug Administration (FDA) for its accelerated approval of SRP-9001/ELEVIDYS for Duchenne muscular dystrophy (DMD) following decades of research in its Center for Gene Therapy to help patients with neuromuscular diseases.
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Discovery of New Form of Dystrophin Protein Could Lead to Therapy for Some DMD Patients
Scientists have discovered a new form of dystrophin, a protein critical to normal muscle function, and identified the genetic mechanism responsible for its production. Studies of the new protein isoform, published online Aug.
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Nationwide Children's Hospital Offers Podcasts Focusing on Neuromuscular Disorders
Scientists and clinicians at Nationwide Children’s Hospital have launched a monthly podcast entitled, “This Month in Muscular Dystrophy,” featuring internationally known scientists discussing the latest research in muscular dystrophy and other neuromuscular disorders.
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Fetal Research Affinity Group
The Fetal Research Affinity Group will bring together experts in fetal therapy, neonatology, genetics, molecular biology and others perinatal fields to develop and advance cutting-edge therapies that can be used to treat fetuses and neonates with a wide range of genetic and medical disorders.
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Perky Jerky® to Support Nationwide Childrens Hospital Beginning in October
Nationwide Children’s Hospital and Perky Jerky® announced today that from October through December, customers at 16 participating Kroger stores will have an opportunity to donate to Nationwide Children’s by purchasing Perky Jerky®.
Specialty
Neuromuscular Disorders
Groundbreaking. Multidisciplinary. Comprehensive. These words don’t just describe our world-class Neuromuscular Disorders program. They are fundamental to our work and the commitment we make to the families who come to us from across the country.
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OTC Events
Learn more about our available technologies and commercialization success stories at our technology showcase events.
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Muscular Dystrophy Research
Dr. Jerry Mendell and his team have discovered that gene therapy can treat the underlying cause of muscular dystrophy - something that other drugs and medications can't currently do.
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Neuromuscular Disorders
Patients benefit from coordinated care from specialists, all with expertise in pediatric neuromuscular disorders.
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MCM-RAG Members
The Molecular and Cellular Medicine-Research Affinity Group is made up of a steering committee and members from both Nationwide Children's Hospital and The Ohio State University. Learn more about its members.
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Nationwide Childrens Hospital Researchers Receive NIH Grant for the Move Toward Clinical Trials Targeting the Lysosomal Storage Disease MPSIIIB
Investigators at Nationwide Children’s have received a grant from the National Institutes of Health (NIH) to help move a therapy for MPS IIIB that has been shown effective in mice toward clinical trials in humans.
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April 2014
Dr. Brian Kaspar discusses a new method for studying ALS, with potential to test therapeutics in individual patients.
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Research Faculty Careers
The Abigail Wexner Research Institute (AWRI) at Nationwide Children’s is ranked among the top 10 freestanding children’s hospitals based on NIH funding. On a continuing trajectory of rapid growth, AWRI is looking for new faculty to drive the next generation of discovery at Nationwide Children's.
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Sarepta Therapeutics Enters Into License Agreement with Nationwide Childrens Hospital for Galgt2 Gene Therapy Program
Sarepta Therapeutics, Inc. (NASDAQ: SRPT), a commercial stage developer of innovative RNA-targeted therapeutics, today announced it has entered a license agreement with Nationwide Children’s Hospital, for their Galgt2 gene therapy program developed by researcher Paul Martin, PhD.
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Endowed Chairs
Endowed chairs at Nationwide Children's Hospital represent the most prestigious and significant recognition of a scientist's or clinician's work.
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Family Foundations Fund Critical Study Necessary For Clinical Trials And Enter Into Agreement With Nationwide Childrens Hospital To Ensure Data Access For Lysosomal Storage Disease MPS III
Nearly 50 years to the day since Dr. Sylvester Sanfilippo first characterized the disease Mucopolysaccharidosis (MPS) III in a presentation to the American Pediatric Society, three parent-run foundations have awarded investigators at Nationwide Children’s Hospital in Columbus, OH with a
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Interprofessional Education and Grand Rounds Update
- Upcoming Conferences
- Pediatric Grand Rounds
- Annual MOC Deadlines
- Lounge and Learn
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Interprofessional Education and Grand Rounds Update
- Project ECHO Q1 2026 Series Preview
- Upcoming Conferences
- Pediatric Grand Rounds
- Annual MOC Deadlines
- Lounge and Learn
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Interprofessional Education and Grand Rounds Update
- Upcoming Conferences
- Pediatric Grand Rounds
- Annual MOC Deadlines
- Lounge and Learn