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Article

March 2015

Dr. Jerry Mendell discusses phase 1/2a follistatin gene therapy trial for becker muscular dystrophy. 

Article

May 2010

Dr. Brian Kaspar discusses gene transfer in spinal muscular atrophy (SMA).

Article

June 2010

Professor Kate Bushby discusses cinical care standards in muscular dystrophy.

Article

February 2011

Dr. Scott Harper discusses DUX4 as a potential candidate gene for facioscapulohumeral muscular dystrophy.

Reading Resources

Are you looking for ways to access free books for your reader? Do you need tips and tricks to grow your child's love for reading? Check out these programs and resources.

Article

February 2015

Dr. Kevin Flanigan discusses IRES-Induced Dystrophin as a potential therapy for DMD.

Article

July 2012

Dr. Louise Rodino-Klapac discusses advances in dysferlin gene therapy.

Article

August 2011

Dr. Valérie Allamand discusses the function of Selenoprotein N in muscle and its link to neuromuscular disorders.

Article

January 2012

Dr. Steve Wilton discusses antisense-induced exon skipping.