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Article
January 2015
Dr. Louise Rodino-Klapac discusses dysferlin overlap vectors to restore function in dysferlinopathies.
Article
July 2011
Dr. Carsten Bonnemann discusses collagen VI myopathies and a novel cause of ullrich congenital muscular dystrophy.
Article
October 2010
Dr. Annemieke Aartsma-Rus discusses progress in antisense oligonucleotide therapies.
Article
April 2010
Gene transfer of follistatin: Dr. Mendell discusses implications for muscle disease.
Article
January 2011
Dr. Jerry Mendell discusses dystrophin immunity in duchenne muscular dystrophy.
Article
July 2013
Dr. Jeff Chamberlain discusses gene and cell mediated therapies for muscular dystrophy.