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Article
September 2011
Dr. Jill Rafael-Fortney discusses the effects of Lisinopril and Spironolactone on DMD mice.
Article
January 2015
Dr. Louise Rodino-Klapac discusses dysferlin overlap vectors to restore function in dysferlinopathies.
Article
Myology Course Archive
Article
June 2011
Dr. Paul Martin discusses how the CMAH gene deletion in the mdx mouse model of duchenne muscular dystrophy helps better mimic the more severe aspects of DMD.
Article
July 2011
Dr. Carsten Bonnemann discusses collagen VI myopathies and a novel cause of ullrich congenital muscular dystrophy.
Article
October 2010
Dr. Annemieke Aartsma-Rus discusses progress in antisense oligonucleotide therapies.
Article
April 2010
Gene transfer of follistatin: Dr. Mendell discusses implications for muscle disease.