Nationwide Children's News Releases

May 28, 2025

Nationwide Children’s Hospital Delivers its First Infusion of CASGEVY™ for Patient with Sickle Cell Disease

Nationwide Children’s Hospital delivered its first commercial infusion of CASGEVY™ to 17-year-old Carlos A. from Dayton, Ohio. Today, Carlos is thriving at home, pain-free.

Feb 03, 2025

Nationwide Children’s Hospital Researcher Receives Grant from the Rosenau Family Research Foundation

The Rosenau Family Research Foundation has awarded a three-year grant of $375,000 total in funding to Allison Bradbury, MS, PhD, along with collaborators at Cincinnati Children’s Hospital Medical Center and Auburn University, for studying in-utero gene therapy as a potential treatment for Krabbe disease and other lysosomal storage diseases.

Nov 07, 2024

Nationwide Children’s Hospital Receives a Wellstone Muscular Dystrophy Specialized Research Center Award from the NIH

Researchers in the Jerry R. Mendell, MD Center for Gene Therapy at Nationwide Children's Hospital have received a coveted P50 grant from the National Institutes of Health to establish a Wellstone Muscular Dystrophy Specialized Research Center (MDSRC).

Nationwide Children’s Hospital Renames Center for Gene Therapy, Honoring Jerry Mendell, MD
Sep 10, 2024

Nationwide Children’s Hospital Renames Center for Gene Therapy, Honoring Jerry Mendell, MD

Nationwide Children’s Hospital announced today the renaming and dedication of the Jerry R. Mendell, MD Center for Gene Therapy at the Abigail Wexner Research Institute, in honor of Jerry Mendell, MD, a pioneer in the fields of neurology and gene therapy and a catalyst for advancement in the treatment of multiple neuromuscular disorders.

Nationwide Children’s Hospital Receives $25 Million Gift to Support Institute for Mental and Behavioral Health Research
Jun 14, 2024

Nationwide Children’s Hospital Receives $25 Million Gift to Support Institute for Mental and Behavioral Health Research

Nationwide Children’s Hospital announced today that longtime donors Joe and Linda Chlapaty have donated $25 million to support the recently launched Institute for Mental and Behavioral Health Research. The gift will fund innovative research, endowed faculty to recruit nationally renowned researchers, and construction for new facilities.

Jerry Mendell, MD, Announced as King Faisal Prize Laureate in Medicine
Jan 18, 2024

Jerry Mendell, MD, Announced as King Faisal Prize Laureate in Medicine

Jerry Mendell, MD, senior advisor in the Center for Gene Therapy in the Abigail Wexner Research Institute at Nationwide Children’s Hospital, is this year’s recipient of the King Faisal Prize for Medicine for his contributions toward the screening, diagnosis and treatment of neuromuscular diseases, including spinal muscular atrophy (SMA), Duchenne muscular dystrophy (DMD) and limb girdle muscular dystrophy.

Dec 11, 2023

Nationwide Children’s Hospital Becomes Authorized Treatment Center for Sickle Cell Gene Therapy

Nationwide Children’s Hospital has been designated an authorized treatment center for CASGEVY™ (exagamglogene autotemcel (exa-cel)), a gene therapy for the treatment of sickle cell disease.

From Bench to Bedside: Patient with Duchenne Muscular Dystrophy Receives First Dose of Gene Therapy Developed at Nationwide Children’s Hospital
Aug 08, 2023

From Bench to Bedside: Patient with Duchenne Muscular Dystrophy Receives First Dose of Gene Therapy Developed at Nationwide Children’s Hospital

In a landmark moment for the Abigail Wexner Research Institute at Nationwide Children’s, a 5-year-old from Bellefontaine, Ohio, received the first dose of a recently approved gene therapy for Duchenne muscular dystrophy at Nationwide Children’s Hospital, where the therapy was invented and initially tested.

Jun 22, 2023

FDA Approves First Gene Therapy Treatment for Duchenne Muscular Dystrophy Developed at the Abigail Wexner Research Institute at Nationwide Children’s Hospital

Today, the Abigail Wexner Research Institute at Nationwide Children’s Hospital praised the Food and Drug Administration (FDA) for its accelerated approval of SRP-9001/ELEVIDYS for Duchenne muscular dystrophy (DMD) following decades of research in its Center for Gene Therapy to help patients with neuromuscular diseases.

May 19, 2023

Nationwide Children’s Hospital Becomes Certified Site for Gene Therapy for Transfusion-Dependent Beta Thalassemia

Nationwide Children’s Hospital has been designated a qualified treatment center for Zynteglo® (betibeglogene autotemcel), a a gene therapy approved for the treatment of people with beta thalassemia who require regular red blood cell transfusions.