Meet Evelyn

No treatment. No cure. These are the words families of children with spinal muscular atrophy (SMA) have always been told upon diagnosis.

Until now.

Now, there is hope for kids with SMA thanks to the work of Dr. Jerry Mendell and the Center for Gene Therapy at the Abigail Wexner Research Institute at Nationwide Children's Hospital. Zolgensma, developed by Dr. Mendell and team in collaboration with colleagues at The Ohio State University, was recently approved by the FDA as the first-ever IV gene therapy.

This is a new era in pediatric research and care, and we are leading the way. Gene therapy breakthroughs taking place at Nationwide Children's are improving and saving lives of children around the world.

Watch Evelyn's story to see how these medical advancements are allowing families like hers to dream again.