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Article

June 2011

Dr. Paul Martin discusses how the CMAH gene deletion in the mdx mouse model of duchenne muscular dystrophy helps better mimic the more severe aspects of DMD.

Article

July 2014

Dr. Scott Harper discusses RNAi silencing in limb girdle muscular dystrophy 1A.

Article

July 2013

Dr. Jeff Chamberlain discusses gene and cell mediated therapies for muscular dystrophy.

Article

July 2012

Dr. Louise Rodino-Klapac discusses advances in dysferlin gene therapy.

Article

September 2012

Professor Francesco Muntoni discusses congenital muscular dystrophies.

Article

March 2012

Dr. Thomas Voit discusses gamma sarcoglycan gene therapy.

Article

June 2013

Dr. Paul Martin discusses Galgt2 gene therapy for muscular dystrophy.

Article

March 2015

Dr. Jerry Mendell discusses phase 1/2a follistatin gene therapy trial for becker muscular dystrophy. 

Article

March 2013

Dr. Louise Rodino-Klapac discusses alpha 7 integrin as A therapeutic approach to muscular dystrophy.

Article

January 2013

Dr. James Ervasti discusses stability of therapeutic forms of dystrophin.

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