Featured Podcasts
March 2015
Dr. Jerry Mendell discusses phase 1/2a follistatin gene therapy trial for becker muscular dystrophy.
February 2015
Dr. Kevin Flanigan discusses IRES-Induced Dystrophin as a potential therapy for DMD.
January 2015
Dr. Louise Rodino-Klapac discusses dysferlin overlap vectors to restore function in dysferlinopathies.
July 2014
Dr. Scott Harper discusses RNAi silencing in limb girdle muscular dystrophy 1A.
2015
March 2015
Dr. Jerry Mendell discusses phase 1/2a follistatin gene therapy trial for becker muscular dystrophy.
February 2015
Dr. Kevin Flanigan discusses IRES-Induced Dystrophin as a potential therapy for DMD.
January 2015
Dr. Louise Rodino-Klapac discusses dysferlin overlap vectors to restore function in dysferlinopathies.
2014
July 2014
Dr. Scott Harper discusses RNAi silencing in limb girdle muscular dystrophy 1A.
April 2014
Dr. Brian Kaspar discusses a new method for studying ALS, with potential to test therapeutics in individual patients.
2013
November 2013
Dr. Louis Chicoine discusses the effect of plasmapheresis in removal of AAV antibodies for gene therapy.
September 2013
Dr. Volker Straub discusses the use of muscle MRI in muscular dystrophy.
July 2013
Dr. Jeff Chamberlain discusses gene and cell mediated therapies for muscular dystrophy.
June 2013
Dr. Paul Martin discusses Galgt2 gene therapy for muscular dystrophy.
March 2013
Dr. Louise Rodino-Klapac discusses alpha 7 integrin as A therapeutic approach to muscular dystrophy.
January 2013
Dr. James Ervasti discusses stability of therapeutic forms of dystrophin.
2012
December 2012
Dr. Federica Montanaro discusses new cardiac dystrophin associated proteins.
September 2012
Professor Francesco Muntoni discusses congenital muscular dystrophies.
July 2012
Dr. Louise Rodino-Klapac discusses advances in dysferlin gene therapy.
May 2012
Dr. Hugh Allen discusses cardiomyopathy in duchenne muscular dystrophy.
April 2012
Dr. Jerry Mendell discusses newborn screening in duchenne muscular dystrophy.
March 2012
Dr. Thomas Voit discusses gamma sarcoglycan gene therapy.
February 2012
Dr. Burghes discusses antisense oligomer treatment in an SMA mouse model.
January 2012
Dr. Steve Wilton discusses antisense-induced exon skipping.
2011
December 2011
Dr. Denis Guttridge discusses NF-kB therapy for duchenne muscular dystrophy.
September 2011
Dr. Jill Rafael-Fortney discusses the effects of Lisinopril and Spironolactone on DMD mice.
August 2011
Dr. Valérie Allamand discusses the function of Selenoprotein N in muscle and its link to neuromuscular disorders.
July 2011
Dr. Carsten Bonnemann discusses collagen VI myopathies and a novel cause of ullrich congenital muscular dystrophy.
June 2011
Dr. Paul Martin discusses how the CMAH gene deletion in the mdx mouse model of duchenne muscular dystrophy helps better mimic the more severe aspects of DMD.
February 2011
Dr. Scott Harper discusses DUX4 as a potential candidate gene for facioscapulohumeral muscular dystrophy.
January 2011
Dr. Jerry Mendell discusses dystrophin immunity in duchenne muscular dystrophy.
2010
December 2010
Dr. Craig McDonald discusses the six-minute walk test as an outcome measure in DMD.
October 2010
Dr. Annemieke Aartsma-Rus discusses progress in antisense oligonucleotide therapies.
September 2010
Dr. Federica Montanaro discusses cardiomyopathy in becker muscular dystrophy.
June 2010
Professor Kate Bushby discusses cinical care standards in muscular dystrophy.
May 2010
Dr. Brian Kaspar discusses gene transfer in spinal muscular atrophy (SMA).
April 2010
Gene transfer of follistatin: Dr. Mendell discusses implications for muscle disease.