Medical Professional Publications

Center for Gene Therapy Scientists Receive Champion of Hope Award for Collaboration in Advocacy

Drs. Kevin Flanigan, Douglas McCarty, and Haiyan Fu—collaborating scientists in Abeona Therapeutics’ Sanfilippo Consortium—received the Champion of Hope Award for Collaboration in Advocacy from Global Genes | RARE Project on September 21.

Tim Miller, President and CEO of Abeona commented: “Your award will not only serve as example of what needs to become the norm within rare disease, but will showcase how collaboration helps to advance efforts for rare disease patients globally."

Global Genes | RARE Project is a leading rare and genetic disease patient advocacy organization. The Foundation's mission is to unify the international rare and genetic disease community by providing connections and resources to ease the burdens of affected patients and their families.  Recognized worldwide by the Blue Denim Genes Ribbon™, Global Genes | RARE Project unites experts, advocates and patients of all ages to stand together in hope for treatments and cures for the 7,000 rare and genetic diseases that impact approximately 30 million Americans and over 250 million people worldwide. For more information, visit

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