Nicolas S Wein, PhD

Nationwide Children's Hospital Medical Professional

Contact Information

Biography
Dr. Wein received his PhD in Molecular Biology in the laboratory of Nicolas Levy, MD, PhD, at the Marseille Medical School in France, where he worked on the development of new diagnosis tools for neuromuscular diseases, the discovery of the Minidysferline and its use for gene transfer, and investigation of the use of exon-skipping for dysferlinopathies. In 2011, he joined the team of Kevin Flanigan, MD, principal investigator in The Center for Gene Therapy at The Research Institute at Nationwide Children's Hospital, as a postdoctoral scientist. Dr. Wein worked on the identification of a novel IRES in the dystrophin gene and on an out-of-frame exon-skipping approach that can benefit patients with 5’ mutations in the DMD gene.
Academic and Clinical Areas
Awards, Honors & Organizations
  • Outstanding Poster Presentation Award, New Directions in Biology and Disease of Skeletal Muscle Conference, Orlando, FL, USA, 2016
  • Outstanding Poster Presentation Award, 19th Annual Meeting of the American Society of Gene and Cell Therapy, Washington, DC, USA, 2016
  • Postdoctoral Scientist of the Year, Nationwide Children's Hospital, 2016
  • Young Investigator Prize, New Directions in Biology and Disease of Skeletal Muscle Conference, Chicago, IL, USA, 2014
  • Outstanding Poster Prize, Muscular Dystrophy Association Scientific Meeting, Washington, DC, 2013
  • Poster Award, 17th International Congress of the World Muscle Society, Perth, Australia, 2013
  • Duchenne Research Award for Best Presentation on Therapy of Duchenne Muscular Dystrophy, 18th International Congress of the World Muscle Society, Asilomar, CA, 2013
  • Young Investigator Prize, 15th International Congress of the World Muscle Society, Kumamoto, Japan, 2012
  • Poster Award, Federative Research Institute 125, Marseille, France, 2010
  • Member, World Muscle Society, 2009 - Present
  • Member, American Society of Gene and Cell Therapy, 2006 - Present
Education

Post Doctoral Center for Gene Therapy at The Research Institute Date Completed: 05/31/2016
Graduate School La Timone Medical School Date Completed: 12/09/2010
Undergraduate School La Timone Medical School Date Completed: 05/30/2006
Clinical Interests
  • Neuromuscular disorders
Professional Experience

2009 - Present World Muscle Society, Member

2006 - Present American Society of Gene and Cell Therapy, Member

Contact Information
Center for Gene Therapy