Neuromuscular Disorders Research :: Nationwide Children's Hospital

Muscular Dystrophy Association's Clinical Research Network

Nationwide Children’s Hospital is one of five centers to be part of the Muscular Dystrophy Association's Clinical Research Network to support trials and studies in Duchenne muscular dystrophy (DMD).

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Neuromuscular Disorders Research

Jerry R. Mendell, MD, Director of the Center for Gene Therapy at The Research Institute at Nationwide Children’s Hospital, is an international leader in the development of innovative treatments for neuromuscular diseases. A primary focus of the Center for Gene Therapy is curing muscular dystrophies and Nationwide Children’s Hospital has been part of the Muscular Dystrophy Association’s Clinical Research Network since 2008. Investigators are currently focused on developing treatments for:

  • Amyotrophic lateral sclerosis (ALS)
  • Becker muscular dystrophy
  • Charcot-Marie-Tooth Neuropathy
  • Duchenne muscular dystrophy
  • Fasioscapulohumeral muscular dystrophy
  • Inclusion body myositis
  • Limb girdle muscular dystrophy type 2D (alpha sarcoglycanopathy)
  • Spinal muscular atrophy

Learn about Heart Research in Neuromuscular Disease, Duchenne Muscular Dystrophy Research and Spinal Muscular Atrophy Research.

Neuromuscular Disorders Research Faculty

Louis Chicoine, MD
Kevin Flanigan, MD
Haiyan Fu, PhD
Scott Harper, PhD
Brian K. Kaspar, PhD
Paul T. Martin, PhD
Douglas M. McCarty, PhD
Jerry R. Mendell, MD
Federica Montanaro, PhD
Louise Rodino-Klapac, PhD
Zarife Sahenk, MD, PhD

Nationwide Children's Hospital
700 Children's Drive Columbus, Ohio 43205 614.722.2000