(From the September 2013 Issue of MedStat)
New research on two promising gene therapies suggests that combining them into one treatment not only repairs muscle damage caused by Duchenne muscular dystrophy, but also prevents future injury from the muscle-wasting disease. The work, led by a team at The Research Institute at Nationwide Children’s Hospital including Louise Rodino-Klapac, PhD, a principle investigator in the Center for Gene Therapy at Nationwide Children’s and lead author of the research, is the first to look at the approach in aged mice, a key step toward clinical trials in patients. The findings were published in July in Human Molecular Genetics.
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