Gene Transfer Clinical Trial for Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)
Phase I/II gene transfer clinical trial for patients with Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) with a study duration of two years and follow-up visits after 1 week, 2 weeks, 1 month, 2 months, 3 months, 6 months, 1 year and 2 years. Read more.
Study for Patients with Duchenne Muscular Dystrophy or Becker Muscular Dystrophy
Patients who are at least 10 years old, have Duchenne Muscular Dystrophy or Becker Muscular Dystrophy, and have a weak heart or a heart device (ex., pacemaker or ICD) are eligible for this non-invasive study, which will collect health information from medical records. Read more.
Infants and Toddlers 9-27 Months Needed for Therapy Study
Infants and young toddlers ages 9-27 months with cerebral palsy who have one side of their body stronger than the other, or those without cerebral palsy and no other motor difficulties, are eligible for this non-invasive, parent-directed therapy study. Read more.